Rare Diseases
Featured Articles : Rare Diseases

January 10, 2019
Supporting rare disease research at NIH
Tiina K. Urv, Ph.D., leads the Rare Diseases Clinical Research Network, part of NIH’s Office of Rare Diseases Research....
Rare Diseases
January 10, 2019
What is it like to research a rare disease?
Andrea L. Gropman, M.D., studies rare diseases with support from NIH and the Rare Diseases Clinical Research Network. She...
Rare Diseases
January 09, 2019
Zoey’s story: One family’s experience with a rare disease
In 2015, college student Zoey Zalusky was 19 years old with an exciting future ahead of her. She had a supportive, loving family,...
Rare Diseases